Sialic Acid Storage Disease [nemoc z ukládání kyseliny sialové]

topical
3
Terms

infantilní forma Sallovy nemoci
kyselina sialová - nemoc z ukládání
lysozomální akumulace volné kyseliny sialové
nemoc Salla
sialurie
sialurie finského typu
sialurie u dětí
střádání kyseliny sialové
střádání kyseliny sialové u dětí

 

French Type Sialuria
Infantile Sialic Acid Storage Disease
Infantile Sialic Acid Storage Disorder
Infantile Sialic Acid Storage Disorder (ISSD)
Salla Disease
Sialic Acid Storage Disease, Finnish Type
Sialic Acid Storage Disease, Infantile Form
Sialuria
Sialuria, Finnish Type
Sialuria, Infantile Form

Persistent link   https://www.medvik.cz/link/D029461
Definition

Autosomal recessive neurodegenerative disorders caused by lysosomal membrane transport defects that result in accumulation of free sialic acid (N-ACETYLNEURAMINIC ACID) within the lysosomes. The two main clinical phenotypes, which are allelic variants of the SLC17A5 gene, are ISSD, a severe infantile form, or Salla disease, a slowly progressive adult form, named for the geographic area in Finland where the kindred first studied resided.

DUI
D029461 MeSH Browser
CUI
M0384694
Previous indexing
Carbohydrate Metabolism, Inborn Errors (1986-2001); Lysosomal Storage Diseases (1991-2001)
History note
2002
Public note
2002

C Diseases
C10.228.140 Brain Diseases 1 177
C10.228.140.163 Brain Diseases, Metabolic 84
C10.228.140.163.100.435.295 Fucosidosis 2
C10.228.140.163.100.435.340 Glycogen Storage Disease Type II 59
C10.228.140.163.100.435.590 Mucolipidoses 10
C10.228.140.163.100.435.810 Sialic Acid Storage Disease 3
C10.228.140.163.100.435.825 Sphingolipidoses 12
C16.320.565.189.435.295 Fucosidosis 2
C16.320.565.189.435.340 Glycogen Storage Disease Type II 59
C16.320.565.189.435.590 Mucolipidoses 10
C16.320.565.189.435.810 Sialic Acid Storage Disease 3
C16.320.565.189.435.825 Sphingolipidoses 12
C16.320.565.595 Lysosomal Storage Diseases 72
C16.320.565.595.554.295 Fucosidosis 2
C16.320.565.595.554.340 Glycogen Storage Disease Type II 59
C16.320.565.595.554.590 Mucolipidoses 10
C16.320.565.595.554.810 Sialic Acid Storage Disease 3
C16.320.565.595.554.825 Sphingolipidoses 12
C18.452 Metabolic Diseases 1 196
C18.452.132.100.435.295 Fucosidosis 2
C18.452.132.100.435.340 Glycogen Storage Disease Type II 59
C18.452.132.100.435.590 Mucolipidoses 10
C18.452.132.100.435.810 Sialic Acid Storage Disease 3
C18.452.132.100.435.825 Sphingolipidoses 12
C18.452.648.189.435.295 Fucosidosis 2
C18.452.648.189.435.340 Glycogen Storage Disease Type II 59
C18.452.648.189.435.590 Mucolipidoses 10
C18.452.648.189.435.810 Sialic Acid Storage Disease 3
C18.452.648.189.435.825 Sphingolipidoses 12
C18.452.648.595 Lysosomal Storage Diseases 72
C18.452.648.595.554.295 Fucosidosis 2
C18.452.648.595.554.340 Glycogen Storage Disease Type II 59
C18.452.648.595.554.590 Mucolipidoses 10
C18.452.648.595.554.810 Sialic Acid Storage Disease 3
C18.452.648.595.554.825 Sphingolipidoses 12