Sandhoff Disease [Sandhoffova nemoc]

topical
1
Terms

GM2 gangliosidóza II
GM2 gangliosidóza, typ II
Sandhoffova nemoc u dospělých
Sandhoffova nemoc, dospělá forma
Sandhoffova nemoc, dospělý typ
Sandhoffova nemoc, infantilní forma
Sandhoffova nemoc, infantilní typ
Sandhoffova nemoc, juvenilní forma
Sandhoffova nemoc, juvenilní typ
úplný deficit hexosaminidázy
úplný nedostatek hexosaminidázy

 

Adult Sandhoff Disease
beta-Hexosaminidase-beta-Subunit Deficiency
Deficiency Disease, Hexosaminidase A and B
G(M2) Gangliosidosis, Type II
Gangliosidosis G(M2), Type II
Gangliosidosis GM2, Type II
GM2 Gangliosidosis, Type 2
GM2 Gangliosidosis, Type II
GM2-Gangliosidosis, Type II
Hexosaminidase A and B Deficiency Disease
Hexosaminidases A And B Deficiency
Infantile Sandhoff Disease
Juvenile Sandhoff Disease
Sandhoff Disease, Adult
Sandhoff Disease, Adult Type
Sandhoff Disease, Infantile
Sandhoff Disease, Infantile Type
Sandhoff Disease, Juvenile
Sandhoff Disease, Juvenile Type
Sandhoff-Jatzkewitz-Pilz Disease
Sandhoff's Disease
Total Hexosaminidase Deficiency

Persistent link   https://www.medvik.cz/link/D012497
Definition

An autosomal recessive neurodegenerative disorder characterized by an accumulation of G(M2) GANGLIOSIDE in neurons and other tissues. It is caused by mutation in the common beta subunit of HEXOSAMINIDASE A and HEXOSAMINIDASE B. Thus this disease is also known as the O variant since both hexosaminidase A and B are missing. Clinically, it is indistinguishable from TAY-SACHS DISEASE.

DUI
D012497 MeSH Browser
CUI
M0019413
Previous indexing
Lipoidosis (1966-1978); Gangliosides (1966-1978); Gangliosidosis (1976-1978); G(M2) Ganglioside (1975-1978); Hexosaminidases (1971-1978); Sphingolipidosis (1974-1978)
History note
1979
Public note
1979

C Diseases
C10.228.140 Brain Diseases 1 178
C10.228.140.163 Brain Diseases, Metabolic 84
C10.228.140.163.100.435.825 Sphingolipidoses 12
C10.228.140.163.100.435.825.300 Gangliosidoses 11
C10.228.140.163.100.435.825.300.300 Gangliosidoses, GM2 2
C10.228.140.163.100.435.825.300.300.249 Sandhoff Disease 1
C10.228.140.163.100.435.825.300.300.500 Tay-Sachs Disease 15
C10.228.140.163.100.435.825.300.300.750 Tay-Sachs Disease, AB Variant
C16.320.565.189.435.825 Sphingolipidoses 12
C16.320.565.189.435.825.300 Gangliosidoses 11
C16.320.565.189.435.825.300.300 Gangliosidoses, GM2 2
C16.320.565.189.435.825.300.300.249 Sandhoff Disease 1
C16.320.565.189.435.825.300.300.500 Tay-Sachs Disease 15
C16.320.565.189.435.825.300.300.750 Tay-Sachs Disease, AB Variant
C16.320.565.398.641 Lipidoses 35
C16.320.565.398.641.803 Sphingolipidoses 12
C16.320.565.398.641.803.350 Gangliosidoses 11
C16.320.565.398.641.803.350.300 Gangliosidoses, GM2 2
C16.320.565.398.641.803.350.300.700 Sandhoff Disease 1
C16.320.565.398.641.803.350.300.850 Tay-Sachs Disease 15
C16.320.565.398.641.803.350.300.925 Tay-Sachs Disease, AB Variant
C16.320.565.595 Lysosomal Storage Diseases 72
C16.320.565.595.554.825 Sphingolipidoses 12
C16.320.565.595.554.825.300 Gangliosidoses 11
C16.320.565.595.554.825.300.300 Gangliosidoses, GM2 2
C16.320.565.595.554.825.300.300.800 Sandhoff Disease 1
C16.320.565.595.554.825.300.300.840 Tay-Sachs Disease 15
C16.320.565.595.554.825.300.300.920 Tay-Sachs Disease, AB Variant
C18.452 Metabolic Diseases 1 196
C18.452.132.100.435.825 Sphingolipidoses 12
C18.452.132.100.435.825.300 Gangliosidoses 11
C18.452.132.100.435.825.300.300 Gangliosidoses, GM2 2
C18.452.132.100.435.825.300.300.249 Sandhoff Disease 1
C18.452.132.100.435.825.300.300.500 Tay-Sachs Disease 15
C18.452.132.100.435.825.300.300.750 Tay-Sachs Disease, AB Variant
C18.452.584.563.641 Lipidoses 35
C18.452.584.563.641.803 Sphingolipidoses 12
C18.452.584.563.641.803.350 Gangliosidoses 11
C18.452.584.563.641.803.350.300 Gangliosidoses, GM2 2
C18.452.584.563.641.803.350.300.700 Sandhoff Disease 1
C18.452.584.563.641.803.350.300.850 Tay-Sachs Disease 15
C18.452.584.563.641.803.350.300.925 Tay-Sachs Disease, AB Variant
C18.452.648.189.435.825 Sphingolipidoses 12
C18.452.648.189.435.825.300 Gangliosidoses 11
C18.452.648.189.435.825.300.300 Gangliosidoses, GM2 2
C18.452.648.189.435.825.300.300.249 Sandhoff Disease 1
C18.452.648.189.435.825.300.300.500 Tay-Sachs Disease 15
C18.452.648.189.435.825.300.300.750 Tay-Sachs Disease, AB Variant
C18.452.648.398.641 Lipidoses 35
C18.452.648.398.641.803 Sphingolipidoses 12
C18.452.648.398.641.803.350 Gangliosidoses 11
C18.452.648.398.641.803.350.300 Gangliosidoses, GM2 2
C18.452.648.398.641.803.350.300.700 Sandhoff Disease 1
C18.452.648.398.641.803.350.300.850 Tay-Sachs Disease 15
C18.452.648.398.641.803.350.300.925 Tay-Sachs Disease, AB Variant
C18.452.648.595 Lysosomal Storage Diseases 72
C18.452.648.595.554.825 Sphingolipidoses 12
C18.452.648.595.554.825.300 Gangliosidoses 11
C18.452.648.595.554.825.300.300 Gangliosidoses, GM2 2
C18.452.648.595.554.825.300.300.800 Sandhoff Disease 1
C18.452.648.595.554.825.300.300.840 Tay-Sachs Disease 15
C18.452.648.595.554.825.300.300.920 Tay-Sachs Disease, AB Variant