Niemann-Pick Disease, Type A [Niemannova-Pickova nemoc typu A]

topical
6
Terms

deficit sfingomyelinázy
nedostatek sfingomyelinázy
Niemann-Pickova nemoc typu A
sfingomyelinasa - nedostatek
sfingomyelinová lipidóza
sfingomyelinóza

 

Classical Niemann-Pick Disease
Neuronal Cholesterol Lipidosis
Niemann-Pick Disease, Acute Neuronopathic Form
Niemann-Pick Disease, Acute Neurovisceral Form
Niemann-Pick Disease, Neuronopathic Type
Niemann-Pick's Disease Type A
Ophthalmoplegia, Supraoptic Vertical
Sphingomyelin Cholesterol Lipidosis
Sphingomyelin Lipidosis
Sphingomyelinase Deficiency
Sphingomyelinase Deficiency Disease
Type A Niemann-Pick Disease

Persistent link   https://www.medvik.cz/link/D052536
Definition

The classic infantile form of Niemann-Pick Disease, caused by mutation in SPHINGOMYELIN PHOSPHODIESTERASE. It is characterized by accumulation of SPHINGOMYELINS in the cells of the MONONUCLEAR PHAGOCYTE SYSTEM and other cell throughout the body leading to cell death. Clinical signs include JAUNDICE, hepatosplenomegaly, and severe brain damage.

DUI
D052536 MeSH Browser
CUI
M0335783
Previous indexing
Niemann-Pick Diseases (1997-2006)
History note
2007; use NIEMANN-PICK DISEASES 2000-2006
Public note
2007; see NIEMANN-PICK DISEASES 2000-2006

C Diseases
C10.228.140 Brain Diseases 1 178
C10.228.140.163 Brain Diseases, Metabolic 84
C10.228.140.163.100.435.825 Sphingolipidoses 12
C10.228.140.163.100.435.825.700 Niemann-Pick Diseases 36
C10.228.140.163.100.435.825.700.500 Niemann-Pick Disease, Type A 6
C10.228.140.163.100.435.825.700.750 Niemann-Pick Disease, Type B 4
C10.228.140.163.100.435.825.700.875 Niemann-Pick Disease, Type C 40
C15.604.250 Histiocytosis 67
C15.604.250.410.625 Niemann-Pick Diseases 36
C15.604.250.410.625.500 Niemann-Pick Disease, Type A 6
C15.604.250.410.625.750 Niemann-Pick Disease, Type B 4
C15.604.250.410.625.875 Niemann-Pick Disease, Type C 40
C16.320.565.189.435.825 Sphingolipidoses 12
C16.320.565.189.435.825.700 Niemann-Pick Diseases 36
C16.320.565.189.435.825.700.500 Niemann-Pick Disease, Type A 6
C16.320.565.189.435.825.700.750 Niemann-Pick Disease, Type B 4
C16.320.565.189.435.825.700.875 Niemann-Pick Disease, Type C 40
C16.320.565.398.641 Lipidoses 35
C16.320.565.398.641.803 Sphingolipidoses 12
C16.320.565.398.641.803.730 Niemann-Pick Diseases 36
C16.320.565.398.641.803.730.500 Niemann-Pick Disease, Type A 6
C16.320.565.398.641.803.730.750 Niemann-Pick Disease, Type B 4
C16.320.565.398.641.803.730.875 Niemann-Pick Disease, Type C 40
C16.320.565.595 Lysosomal Storage Diseases 72
C16.320.565.595.554.825 Sphingolipidoses 12
C16.320.565.595.554.825.700 Niemann-Pick Diseases 36
C16.320.565.595.554.825.700.500 Niemann-Pick Disease, Type A 6
C16.320.565.595.554.825.700.750 Niemann-Pick Disease, Type B 4
C16.320.565.595.554.825.700.875 Niemann-Pick Disease, Type C 40
C18.452 Metabolic Diseases 1 196
C18.452.132.100.435.825 Sphingolipidoses 12
C18.452.132.100.435.825.700 Niemann-Pick Diseases 36
C18.452.132.100.435.825.700.500 Niemann-Pick Disease, Type A 6
C18.452.132.100.435.825.700.750 Niemann-Pick Disease, Type B 4
C18.452.132.100.435.825.700.875 Niemann-Pick Disease, Type C 40
C18.452.584.563.641 Lipidoses 35
C18.452.584.563.641.803 Sphingolipidoses 12
C18.452.584.563.641.803.730 Niemann-Pick Diseases 36
C18.452.584.563.641.803.730.500 Niemann-Pick Disease, Type A 6
C18.452.584.563.641.803.730.750 Niemann-Pick Disease, Type B 4
C18.452.584.563.641.803.730.875 Niemann-Pick Disease, Type C 40
C18.452.648.189.435.825 Sphingolipidoses 12
C18.452.648.189.435.825.700 Niemann-Pick Diseases 36
C18.452.648.189.435.825.700.500 Niemann-Pick Disease, Type A 6
C18.452.648.189.435.825.700.750 Niemann-Pick Disease, Type B 4
C18.452.648.189.435.825.700.875 Niemann-Pick Disease, Type C 40
C18.452.648.398.641 Lipidoses 35
C18.452.648.398.641.803 Sphingolipidoses 12
C18.452.648.398.641.803.730 Niemann-Pick Diseases 36
C18.452.648.398.641.803.730.500 Niemann-Pick Disease, Type A 6
C18.452.648.398.641.803.730.750 Niemann-Pick Disease, Type B 4
C18.452.648.398.641.803.730.875 Niemann-Pick Disease, Type C 40
C18.452.648.595 Lysosomal Storage Diseases 72
C18.452.648.595.554.825 Sphingolipidoses 12
C18.452.648.595.554.825.700 Niemann-Pick Diseases 36
C18.452.648.595.554.825.700.500 Niemann-Pick Disease, Type A 6
C18.452.648.595.554.825.700.750 Niemann-Pick Disease, Type B 4
C18.452.648.595.554.825.700.875 Niemann-Pick Disease, Type C 40