Mucopolysaccharidosis I [mukopolysacharidóza I]

topical
29
Terms

deficit alfa-L-iduronidasy
deficit alfa-L-iduronidázy
deficit α-L-iduronidasy
gargoylismus
lipochondrodystrofie
mukopolysacharidóza I-S
mukopolysacharidóza I. typu
mukopolysacharidóza IH
mukopolysacharidóza typu I
mukopolysacharidóza V
mukopolysacharidóza V. typu
Scheieův syndrom
syndrom Hurlerové
syndrom Hurlerové-Scheieův
syndrom Scheieův

 

alpha-L-Iduronidase Deficiency
Gargoylism
Gargoylism, Hurler Syndrome
Hurler Disease
Hurler Syndrome
Hurler-Scheie Syndrome
Hurler's Disease
Hurler's Syndrome
Lipochondrodystrophy
Mucopolysaccharidosis 1
Mucopolysaccharidosis 5
Mucopolysaccharidosis I-S
Mucopolysaccharidosis Type I
Mucopolysaccharidosis Type Ih
Mucopolysaccharidosis Type Ih S
Mucopolysaccharidosis Type Is
Mucopolysaccharidosis V
Pfaundler-Hurler Syndrome
Scheie Syndrome
Scheie's Syndrome

Persistent link   https://www.medvik.cz/link/D008059
Definition

A group of autosomal recessive lysosomal storage disorders caused by mutations in the gene encoding the enzyme, alpha-L-iduronidase (IDUA), required for the degradation of heparan and dermatan sulfates. This leads to abnormal accumulation of these glycosaminoglycans in various tissues causing a wide range of clinical presentations including cognitive and musculoskeletal disorders.

DUI
D008059 MeSH Browser
CUI
M0012558
History note
1992; use LIPOCHONDRODYSTROPHY 1966-1991; MUCOPOLYSACCHARIDOSIS 5 was heading 1991, use MUCOPOLYSACCHARIDOSIS 1975-1990; for MUCOPOLYSACCHARIDOSIS 1 use LIPOCHONDRODYSTROPHY 1976-1991; for HURLER'S DISEASE use LIPOCHONDRODYSTROPHY 1975-1991; for SCHEIE'S SYNDROME use MUCOPOLYSACCHARIDOSIS 5 1975-1991;
Public note
1992; see LIPOCHONDRODYSTROPHY 1966-91; MUCOPOLYSACCHARIDOSIS 5 was heading 1991, see MUCOPOLYSACCHARIDOSIS 1975-1990; for MUCOPOLYSACCHARIDOSIS 1 see LIPOCHONDRODYSTROPHY 1976-1991; for HURLER'S DISEASE see LIPOCHONDRODYSTROPHY 1975-1991; for SCHEIE'S SYNDROME see MUCOPOLYSACCHARIDOSIS 5 1975-1991

C Diseases
C16.320.565.202.715 Mucopolysaccharidoses 81
C16.320.565.202.715.640 Mucopolysaccharidosis I 29
C16.320.565.202.715.645 Mucopolysaccharidosis II 25
C16.320.565.202.715.650 Mucopolysaccharidosis III 10
C16.320.565.202.715.655 Mucopolysaccharidosis IV 13
C16.320.565.202.715.670 Mucopolysaccharidosis VI 8
C16.320.565.202.715.675 Mucopolysaccharidosis VII 1
C16.320.565.595 Lysosomal Storage Diseases 72
C16.320.565.595.600 Mucopolysaccharidoses 81
C16.320.565.595.600.640 Mucopolysaccharidosis I 29
C16.320.565.595.600.645 Mucopolysaccharidosis II 25
C16.320.565.595.600.650 Mucopolysaccharidosis III 10
C16.320.565.595.600.655 Mucopolysaccharidosis IV 13
C16.320.565.595.600.670 Mucopolysaccharidosis VI 8
C16.320.565.595.600.675 Mucopolysaccharidosis VII 1
C17.300.550 Mucinoses 17
C17.300.550.575 Mucopolysaccharidoses 81
C17.300.550.575.640 Mucopolysaccharidosis I 29
C17.300.550.575.645 Mucopolysaccharidosis II 25
C17.300.550.575.650 Mucopolysaccharidosis III 10
C17.300.550.575.655 Mucopolysaccharidosis IV 13
C17.300.550.575.670 Mucopolysaccharidosis VI 8
C17.300.550.575.675 Mucopolysaccharidosis VII 1
C18.452 Metabolic Diseases 1 196
C18.452.648.202.715 Mucopolysaccharidoses 81
C18.452.648.202.715.640 Mucopolysaccharidosis I 29
C18.452.648.202.715.645 Mucopolysaccharidosis II 25
C18.452.648.202.715.650 Mucopolysaccharidosis III 10
C18.452.648.202.715.655 Mucopolysaccharidosis IV 13
C18.452.648.202.715.670 Mucopolysaccharidosis VI 8
C18.452.648.202.715.675 Mucopolysaccharidosis VII 1
C18.452.648.595 Lysosomal Storage Diseases 72
C18.452.648.595.600 Mucopolysaccharidoses 81
C18.452.648.595.600.640 Mucopolysaccharidosis I 29
C18.452.648.595.600.645 Mucopolysaccharidosis II 25
C18.452.648.595.600.650 Mucopolysaccharidosis III 10
C18.452.648.595.600.655 Mucopolysaccharidosis IV 13
C18.452.648.595.600.670 Mucopolysaccharidosis VI 8
C18.452.648.595.600.675 Mucopolysaccharidosis VII 1