Fucosidosis [fukosidóza]

topical
2
Terms

fukosidóza, infantilní forma
fukosidóza, juvenilní forma
fukosidóza, typ 1
fukosidóza, typ 2
fukosidóza, typ I
fukosidóza, typ II
infantilní fukosidóza
juvenilní fukosidóza

 

Alpha-Fucosidase Deficiency
alpha-Fucosidase Deficiency Disease
alpha-L-Fucosidase Deficiency
alpha-L-Fucosidase Deficiency Disease
Deficiency Disease, alpha-Fucosidase
Deficiency Disease, alpha-L-Fucosidase
Fucosidase Deficiency
Fucosidase Deficiency Disease
Fucosidosis Type 1
Fucosidosis Type I
Fucosidosis Type II
Fucosidosis, Infantile
Fucosidosis, Juvenile

Persistent link   https://www.medvik.cz/link/D005645
Definition

An autosomal recessive lysosomal storage disease caused by a deficiency of ALPHA-L-FUCOSIDASE activity resulting in an accumulation of fucose containing SPHINGOLIPIDS; GLYCOPROTEINS, and mucopolysaccharides (GLYCOSAMINOGLYCANS) in lysosomes. The infantile form (type I) features psychomotor deterioration, MUSCLE SPASTICITY, coarse facial features, growth retardation, skeletal abnormalities, visceromegaly, SEIZURES, recurrent infections, and MACROGLOSSIA, with death occurring in the first decade of life. Juvenile fucosidosis (type II) is the more common variant and features a slowly progressive decline in neurologic function and angiokeratoma corporis diffusum. Type II survival may be through the fourth decade of life. (From Menkes, Textbook of Child Neurology, 5th ed, p87; Am J Med Genet 1991 Jan;38(1):111-31)

DUI
D005645 MeSH Browser
CUI
M0008875
Previous indexing
Carbohydrate Metabolism, Inborn Errors (1966-1984); Fucose (1966-1984); Fucosidase (1975-1984)
History note
1985
Public note
1985

C Diseases
C10.228.140 Brain Diseases 1 177
C10.228.140.163 Brain Diseases, Metabolic 84
C10.228.140.163.100.435.295 Fucosidosis 2
C10.228.140.163.100.435.340 Glycogen Storage Disease Type II 59
C10.228.140.163.100.435.590 Mucolipidoses 10
C10.228.140.163.100.435.810 Sialic Acid Storage Disease 3
C10.228.140.163.100.435.825 Sphingolipidoses 12
C16.320.565.189.435.295 Fucosidosis 2
C16.320.565.189.435.340 Glycogen Storage Disease Type II 59
C16.320.565.189.435.590 Mucolipidoses 10
C16.320.565.189.435.810 Sialic Acid Storage Disease 3
C16.320.565.189.435.825 Sphingolipidoses 12
C16.320.565.202.303 Fucosidosis 2
C16.320.565.202.355 Galactosemias 44
C16.320.565.202.449 Glycogen Storage Disease 44
C16.320.565.202.460 Hyperoxaluria, Primary 9
C16.320.565.202.589 Lactose Intolerance 132
C16.320.565.202.607 Mannosidase Deficiency Diseases 1
C16.320.565.202.670 Mucolipidoses 10
C16.320.565.202.715 Mucopolysaccharidoses 81
C16.320.565.595 Lysosomal Storage Diseases 72
C16.320.565.595.554.295 Fucosidosis 2
C16.320.565.595.554.340 Glycogen Storage Disease Type II 59
C16.320.565.595.554.590 Mucolipidoses 10
C16.320.565.595.554.810 Sialic Acid Storage Disease 3
C16.320.565.595.554.825 Sphingolipidoses 12
C18.452 Metabolic Diseases 1 196
C18.452.132.100.435.295 Fucosidosis 2
C18.452.132.100.435.340 Glycogen Storage Disease Type II 59
C18.452.132.100.435.590 Mucolipidoses 10
C18.452.132.100.435.810 Sialic Acid Storage Disease 3
C18.452.132.100.435.825 Sphingolipidoses 12
C18.452.648.189.435.295 Fucosidosis 2
C18.452.648.189.435.340 Glycogen Storage Disease Type II 59
C18.452.648.189.435.590 Mucolipidoses 10
C18.452.648.189.435.810 Sialic Acid Storage Disease 3
C18.452.648.189.435.825 Sphingolipidoses 12
C18.452.648.202.303 Fucosidosis 2
C18.452.648.202.355 Galactosemias 44
C18.452.648.202.449 Glycogen Storage Disease 44
C18.452.648.202.460 Hyperoxaluria, Primary 9
C18.452.648.202.589 Lactose Intolerance 132
C18.452.648.202.607 Mannosidase Deficiency Diseases 1
C18.452.648.202.670 Mucolipidoses 10
C18.452.648.202.715 Mucopolysaccharidoses 81
C18.452.648.595 Lysosomal Storage Diseases 72
C18.452.648.595.554.295 Fucosidosis 2
C18.452.648.595.554.340 Glycogen Storage Disease Type II 59
C18.452.648.595.554.590 Mucolipidoses 10
C18.452.648.595.554.810 Sialic Acid Storage Disease 3
C18.452.648.595.554.825 Sphingolipidoses 12